← Diseases|Hemophilia A

Hemophilia A

56 programs · 55 companies

Programs
56
Companies
55
Trials
57
MOAs
36
KIF18AiALKiIL-13iCD47iTNFiBTKiPCSK9iIL-17iHPK1iBCMA ADC
Drugs
DrugCompanyPhaseTargetMOA
PexatenlimabNovartisPhase 1/2GPRC5DKIF18Ai
BMY-2495Bristol-Myers SquibbPhase 3KRASG12DALKi
GozesotorasibBristol-Myers SquibbNDA/BLAHER2IL-13i
ZenonesiranGSKPreclinicalDLL3CD47i
TAK-8262TakedaNDA/BLATauTNFi
DSN-5254Daiichi SankyoPhase 1B7-H3ALKi
BMR-8377BioMarinPhase 1/2PCSK9BTKi
MavutuximabHansoh PharmaPhase 2/3PI3KαPCSK9i
NidaratamabKrystal BiotechPreclinicalRETIL-17i
COR-9566CorceptApprovedTYK2HPK1i
TerazumabRecursionPhase 3AHRBCMA ADC
CGO-2579CG OncologyApprovedTIGITRAS(ON)i
SLD-2973Solid BioNDA/BLAKIF18APCSK9i
CSL-7919CSL LimitedPreclinicalBTKPLK4i
RilutenlimabOtsukaPhase 2GIP-RFXIai
VoxarapivirZai LabPhase 2GPRC5DCAR-T CD19
SAM-IIT-777Samsung Medical CtrPhase 1PLK4WEE1i
EOR-IIT-912EORTCPhase 1TNFαCAR-T CD19
UCL-IIT-448UCLA HealthPhase 1PD-L1PD-L1i
INS-6048Insilico MedicineNDA/BLACD20Anti-Aβ
ElraratamabErascaPhase 1PCSK9FGFRi
ACO-697ACLARIONPhase 1/2TIM-3WRNi
MirisotorasibZevra TherapeuticsPhase 1/2PRMT5ALKi
CAL-4725Calithera BioPreclinicalWEE1SGLT2i
MavucageneAthenexPhase 1/2VEGFAHRant
AdagrafotisoranMiNT TherapeuticsPhase 2/3IL-17APCSK9i
MNO-1564MediciNovaPhase 3B7-H3IL-13i
PolalemzoparlimabBioNova PharmaPhase 1/2SMN2IL-17i
PemifutibatinibKelun-BiotechPhase 3BETFXIai
BIG-3814BigHat BioApprovedWRNGLP-1ag
OCT-7288Octant BioPhase 2/3CD123Menini
NiralemzoparlimabGenerate BioPhase 2/3SOS1MDM2i
OlpanaritideBioHaven (Pfizer)Phase 2/3CGRPFXIai
IVE-3532Iveric (Astellas)Phase 1CDK2EZH2i
FRE-IIT-416Fred HutchPhase 2TROP-2CGRPant
418-9392Mitsubishi TanabeNDA/BLAMALT1PCSK9i
BemasacituzumabTaiho PharmaPhase 1/2TROP-2CFTRmod
618-5050CanSinoPhase 2IL-17ACAR-T CD19
LirazasiranVectura (PMI)Phase 3KRASG12DKRASG12Ci
LisonaritideHansa BioPreclinicalCD20ALKi
BemavorutinibMerck KGaAPreclinicalPCSK9CD3xCD20
RCE-2070Avita MedicalPhase 1/2FGFRBCL-2i
NYK-4396Vaccibody (Nykode)PreclinicalPD-L1EGFRi
DatozanubrutinibHanmi PharmPhase 2CGRPCAR-T BCMA
MavulucimabTecnoquimicasNDA/BLACGRPPCSK9i
PolalemzoparlimabNobel IlacApprovedGPRC5DWEE1i
ASA-IIT-449Asan Medical CenterApprovedFLT3SGLT2i
FUD-IIT-133Fudan Cancer HospPhase 1/2VEGFCD3xCD20
RUI-IIT-267Ruijin HospitalApprovedPD-L1BiTE
NAT-IIT-211Natl Taiwan Univ HospPhase 3AuroraAEGFRi
CTT-403CTTQ PharmaPhase 1JAK2BCMA ADC
600-3422Zhejiang HisunPhase 1KRASG12DBETi
TirasertibAvantorPhase 2/3IL-13STINGag
EUP-4341Eupraxia PharmaPreclinicalTIM-3TNFi
RiluzumabZoetisApprovedSHP2CAR-T CD19
CevivorutinibMedPactoPhase 2/3KIF18AHER2
Trials (57)
NCTDrugPhaseStatus
NCT06974514PexatenlimabPhase 1/2Completed
NCT05368713GozesotorasibNDA/BLANot yet recr...
NCT06285794GozesotorasibNDA/BLARecruiting
NCT04907615ZenonesiranPreclinicalCompleted
NCT06847866TAK-8262NDA/BLANot yet recr...
NCT03572481TAK-8262NDA/BLACompleted
NCT05255097DSN-5254Phase 1Not yet recr...
NCT04124487DSN-5254Phase 1Completed
NCT03453657MavutuximabPhase 2/3Recruiting
NCT08533319MavutuximabPhase 2/3Not yet recr...
NCT03973894NidaratamabPreclinicalRecruiting
NCT05862647NidaratamabPreclinicalTerminated
NCT04104768TerazumabPhase 3Not yet recr...
NCT05649699CGO-2579ApprovedTerminated
NCT07839774CGO-2579ApprovedRecruiting
NCT07230849CGO-2579ApprovedCompleted
NCT03406222SLD-2973NDA/BLANot yet recr...
NCT04759861RilutenlimabPhase 2Not yet recr...
NCT03471954VoxarapivirPhase 2Recruiting
NCT07890561SAM-IIT-777Phase 1Active