PCSK9
41 programs · 38 companies
Programs
41
Companies
38
Active Trials
33
Targeting PCSK9
| Drug | Company | Phase | MOA | Indications |
|---|---|---|---|---|
| Zanusertib | AbbVie | Approved | AMLRett | |
| GIL-4361 | Gilead Sciences | Preclinical | Gastric CaHNSCC | |
| REG-2172 | Regeneron | Phase 1/2 | Wilms | |
| BMR-8377 | BioMarin | Phase 1/2 | MSHemophilia A | |
| Capifutibatinib | Incyte | Phase 3 | MigraineMCL | |
| INC-5849 | Incyte | Phase 2 | MMPsoriasis | |
| Talatapinarof | Samsung Biologics | Phase 1/2 | MelanomaFSGS | |
| Sovaglumide | Chugai | Phase 3 | OCDThymoma | |
| Gelibrutinib | Otsuka | Phase 1 | FL | |
| Mavurasimod | Imugene | Phase 2 | GBMAsthma | |
| NIA-IIT-852 | NIAID | NDA/BLA | Wilms | |
| EOR-IIT-940 | EORTC | Phase 3 | FSGS | |
| Elraratamab | Erasca | Phase 1 | Hemophilia AEndometrial Ca | |
| Motarasimod | Replicate Bio | Phase 2 | MGBreast Ca | |
| Lirasacituzumab | MBX Bio | Preclinical | ADPKDIgAN | |
| CRB-4064 | Corbus Pharma | NDA/BLA | MM | |
| LUC-2815 | Lucid Diagnostics | Phase 1 | GARett | |
| MEI-1770 | MEI Pharma | Phase 2/3 | SLEHeart Failure | |
| CYD-4746 | CytoDyn | Phase 1 | DMDBladder Ca | |
| Voxazanubrutinib | Achilles Therapeutics | Phase 1/2 | MigraineObesity | |
| ACR-6734 | Aclaris Therapeutics | Approved | RCC | |
| KTO-5045 | Kitov Pharma | Approved | RCCALS | |
| 269-6259 | Henlius | Phase 3 | SCLCACC | |
| Rimanaritide | Evommune | Phase 1 | PTSD | |
| Adagrafutibatinib | Soleno Ther | Phase 3 | IPFCrohn's | |
| Elralucimab | Zydus Life | Phase 1 | DMDBladder Ca | |
| Nidaosocimab | Genus | Phase 1 | RBMDD | |
| Capibrutinib | Merck KGaA | NDA/BLA | Celiac | |
| MRK-474 | Merck KGaA | Phase 3 | UCGastric Ca | |
| Bemavorutinib | Merck KGaA | Preclinical | CKDHemophilia A | |
| Darasotorasib | Knight Ther | Preclinical | ALS | |
| Zoriratamab | Exact Sciences | Phase 2/3 | NMOSDMyelofibrosis | |
| VVY-8289 | Vivoryon | Phase 2/3 | NASH | |
| MIN-2764 | MiNA Therapeutics | Phase 3 | PompeSLE | |
| BRK-5301 | Bruker | Preclinical | Cholangiocarcinoma | |
| WST-9696 | West Pharma | Phase 3 | FabryBladder Ca | |
| ZEN-2386 | Zentiva | Phase 3 | Gastric CaFTD | |
| LEO-5676 | LEO Pharma | Phase 2/3 | MS | |
| THE-8498 | Theramex | Preclinical | CLLDLBCL | |
| ZYM-7222 | Zymergen (Ginkgo) | Approved | Cervical Ca | |
| Datozumab | GNI Group | Phase 1/2 | Alzheimer'sCRC |