Diseases (100)

IndicationProgramsCompaniesTrials
Pompe827968
NB787576
LGS746972
FSGS737245
Endometrial Ca726866
HS696764
Celiac696658
Schizophrenia686553
Bladder Ca676674
PBC676553
Heart Failure666354
PNH666548
RB666350
SMA656262
MG656468
MCL656159
LN656262
Parkinson's646359
Migraine646458
OCD646365
MS636252
RSV636239
IPF625867
FTD626175
CLL616053
Psoriasis616059
HNSCC615949
HCC615949
GBM615553
CF615849
CKD616056
MDS605849
AS605846
Thymoma606055
MM595555
T2D595856
NMOSD595864
ADPKD595866
Ovarian Ca585853
MDD585850
TTR Amyloidosis585636
Fabry585546
Rett585756
Wilms585356
Prostate Ca575655
Crohn's575645
FL575546
Urothelial Ca575243
Angelman575540
CSU575753
EoE575746
MCC575544
Ewing Sarcoma575459
DLBCL565555
SCD565457
Hemophilia A565557
SCLC565347
Huntington's565561
Dravet565447
CML565356
NSCLC555544
Melanoma555569
RA555257
GA555252
PsA555358
PSP555349
CTCL555351
Meso555542
NASH545247
Asthma545145
PV545353
PAH545251
ADHD545340
Cervical Ca545457
ACC545246
CRC535250
SLE535242
Obesity535244
ALL535149
Gastric Ca525243
AML515046
UC515045
Epilepsy514944
BCC514947
RCC504746
GIST504743
Cholangiocarcinoma494643
Breast Ca484747
DMD484437
ALS484641
Myelofibrosis484734
IgAN474641
ET474743
WM474645
Pancreatic Ca464642
Wet AMD464535
Narcolepsy464434
Atopic Derm434340
PTSD434335
Alzheimer's353535