BM
BioMarin
BMRN·NASDAQSan Rafael CAFounded 19973,500 employees
Large CapbiotechPublicRare DiseaseGenetic MedicineHematology
Platform: ERT & Gene
Market Cap
$16B
All Drugs
6
Clinical Trials
11
Failed / Terminated
2
FDA Approved
0
Stock Price & Catalysts (BMRN)
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Drug Pipeline (6 programs)
| Drug Name | Code | Phase | Trials | Modality | Target | MOA | Indications |
|---|---|---|---|---|---|---|---|
| BMR-9762 | BMR-9762 | Phase 3 | 4 | Aβ | Psoriasis | ||
| Sovarelsin | BMR-1858 | Phase 2 | 1 | CFTR | PSP | ||
| Daratuximab | BMR-4242 | Phase 1 | 2 | PRMT5 | Prostate CaNarcolepsy | ||
| BMR-8526 | BMR-8526 | Phase 1/2 | 1 | CD38 | AS | ||
| BMR-8377 | BMR-8377 | Phase 1/2 | 1 | PCSK9 | MSHemophilia A | ||
| BMR-1165 | BMR-1165 | Phase 2 | 2 | CD47 | GAIPF |
SEC Filings & Financial Documents
Insider Trading Activity
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Catalyst Events (8)