← Pipeline|Tiramavacamten

Tiramavacamten

Preclinical
RHH-3023
Source: Trial-derived·Trials: 2
Modality
Degrader
MOA
PI3Ki
Target
SGLT2
Pathway
Cell Cycle
SchizophreniaMesoRSV
Development Pipeline
Preclinical
Mar 2019
Jan 2030
PreclinicalCurrent
NCT04020868
1,764 pts·Meso
2019-032027-09·Completed
NCT04775695
152 pts·Schizophrenia
2021-122030-01·Terminated
1,916 total pts2 indications
Phase 1
Phase 2
Phase 3
NDA/BLA
Approved
CompletedCurrentUpcoming
Catalysts (2)
2027-09-261.5y awayInterim· Meso
2030-01-133.8y awayInterim· Schizophrenia
Trial Timeline
2019Q2Q3Q42020Q2Q3Q42021Q2Q3Q42022Q2Q3Q42023Q2Q3Q42024Q2Q3Q42025Q2Q3Q42026Q2Q3Q42027Q2Q3Q42028Q2Q3Q42029Q2Q3Q42030Q2
Preclinical
Complet…
Preclinical
Termina…
Catalysts
Interim
2027-09-26 · 1.5y away
Meso
Interim
2030-01-13 · 3.8y away
Schizophrenia
CompletedTerminated|StartCompletionToday
Trials (2)
NCTPhaseIndicationStatusNEP
NCT04020868PreclinicalMesoCompleted1764Biomarker
NCT04775695PreclinicalSchizophreniaTerminated152SRI-4
Competitors (10)
DrugCompanyPhaseTargetMOA
RHH-7558RochePhase 1SGLT2Anti-Tau
NVS-5126NovartisPhase 3SHP2PI3Ki
VoxacilimabAstraZenecaPhase 1/2GLP-1RPI3Ki
CapifutibatinibSanofiApprovedPRMT5PI3Ki
RimatenlimabNovo NordiskPhase 2/3SGLT2PI3Ki
DSN-7360Daiichi SankyoApprovedSGLT2BiTE
REG-3155RegeneronPhase 1/2MDM2PI3Ki
SRP-3270SareptaPhase 1/2SGLT2PI3Ki
TirarapivirUnited TherapeuticsApprovedSGLT2CD47i
PexanaritideInnovent BioPreclinicalSGLT2USP1i