SR

Sarepta

SRPT·NASDAQCambridge MAFounded 19802,800 employees
Large CapbiotechPublicRare DiseaseGenetic Medicine
Platform: Gene Ther RNA
Market Cap
$14B
All Drugs
5
Clinical Trials
10
Failed / Terminated
2
FDA Approved
0
Stock Price & Catalysts (SRPT)
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Drug Pipeline (5 programs)
Drug NameCodePhaseTrialsModalityTargetMOAIndications
SRP-9822SRP-9822Phase 34mAbSOS1FGFRiBCCCRC
SRP-1135SRP-1135Phase 2/31Gene TherapyMDM2PD-L1iMigraine
SRP-3270SRP-3270Phase 1/22Gene TherapySGLT2PI3KiLGS
PeminaritideSRP-3034NDA/BLA2DegraderPLK4JAK1/2iT2DPNH
PemiinavolisibSRP-4631NDA/BLA1siRNACD47GLP-1/GIPCTCLPBC
SEC Filings & Financial Documents
Insider Trading Activity
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Catalyst Events (10)
2025-01-18
SRP-9822 Ph3 Readout
CRC
Past
2025-05-14
SRP-3270 Ph2 Data
LGS
Past
2025-10-25
Peminaritide Ph3 Readout
PNH
Past
2025-11-07
Pemiinavolisib Ph3 Readout
PBC
Past
2026-09-25
SRP-9822 Ph3 Readout
BCC
Ph3 Readout
2027-01-16
Peminaritide Ph3 Readout
PNH
Ph3 Readout
2029-04-24
SRP-9822 Ph3 Readout
BCC
Ph3 Readout
2029-10-19
SRP-9822 Ph3 Readout
BCC
Ph3 Readout
2030-10-01
SRP-3270 Ph2 Data
LGS
Ph2 Data
2031-11-26
SRP-1135 Ph3 Readout
Migraine
Ph3 Readout