← Pipeline|Tirafotisoran

Tirafotisoran

Phase 2
RHH-2139
Source: Trial-derived·Trials: 2
Modality
Vaccine
MOA
CDK2i
Target
CD38
Pathway
STING
AngelmanPNHGA
Development Pipeline
Preclinical
~Feb 2015
~May 2016
Phase 1
~Aug 2016
~Nov 2017
Phase 2
Feb 2018
Sep 2031
Phase 2Current
NCT03620071
1,423 pts·GA
2018-022031-09·Active
NCT04854579
2,761 pts·GA
2023-032025-11·Terminated
4,184 total pts1 indication
Phase 3
NDA/BLA
Approved
CompletedCurrentUpcoming
Catalysts (2)
2025-11-105mo agoPh2 Data· GA
2031-09-285.5y awayPh2 Data· GA
Trial Timeline
2018Q2Q3Q42019Q2Q3Q42020Q2Q3Q42021Q2Q3Q42022Q2Q3Q42023Q2Q3Q42024Q2Q3Q42025Q2Q3Q42026Q2Q3Q42027Q2Q3Q42028Q2Q3Q42029Q2Q3Q42030Q2Q3Q42031Q2Q3Q4
P2
Active
P2
Termina…
Catalysts
Ph2 Data
2025-11-10 · 5mo ago
GA
Ph2 Data
2031-09-28 · 5.5y away
GA
ActiveTerminated|StartCompletionToday
Trials (2)
NCTPhaseIndicationStatusNEP
NCT03620071Phase 2GAActive1423HAM-D
NCT04854579Phase 2GATerminated2761eGFR
Competitors (10)
DrugCompanyPhaseTargetMOA
PFE-3703PfizerPhase 1/2CDK2CDK2i
TerafutibatinibPfizerPhase 1/2CD38CGRPant
NVS-6360NovartisApprovedCD38FXIai
DoxasotorasibAbbViePhase 2CD38VEGFi
ABB-3951AbbViePhase 2/3TNFαCDK2i
AZN-6870AstraZenecaPhase 2/3EGFRCDK2i
SNY-2289SanofiPhase 2/3CD38IL-17i
NVO-1361Novo NordiskPhase 3CD38CD3xCD20
TirasotorasibTakedaNDA/BLAIL-17ACDK2i
MavuglumideBayerApprovedGLP-1RCDK2i