← Pipeline|Ribozasiran

Ribozasiran

Phase 2/3
HTG-4852
Source: Trial-derived·Trials: 2
Modality
ASO
MOA
CAR-T CD19
Target
B7-H3
Pathway
STING
RCCNASH
Development Pipeline
Preclinical
~Oct 2015
~Jan 2017
Phase 1
~Apr 2017
~Jul 2018
Phase 2
Oct 2018
May 2030
Phase 2Current
NCT07278194
2,934 pts·NASH
2018-10TBD·Terminated
NCT03825744
2,435 pts·RCC
2023-012030-05·Active
5,369 total pts2 indications
Phase 3
NDA/BLA
Approved
CompletedCurrentUpcoming
Catalysts (1)
2030-05-174.1y awayPh3 Readout· RCC
Trial Timeline
Q42019Q2Q3Q42020Q2Q3Q42021Q2Q3Q42022Q2Q3Q42023Q2Q3Q42024Q2Q3Q42025Q2Q3Q42026Q2Q3Q42027Q2Q3Q42028Q2Q3Q42029Q2Q3Q42030Q2Q3
P2/3
Termina…
P2/3
Active
Catalysts
Ph3 Readout
2030-05-17 · 4.1y away
RCC
ActiveTerminated|StartCompletionToday
Trials (2)
NCTPhaseIndicationStatusNEP
NCT07278194Phase 2/3NASHTerminated2934UPCR
NCT03825744Phase 2/3RCCActive2435VA
Competitors (10)
DrugCompanyPhaseTargetMOA
LLY-4358Eli LillyPhase 3B7-H3CFTRmod
RHH-1546RochePhase 2/3C5CAR-T CD19
CeviglumideRocheNDA/BLAB7-H3CD47i
DatoglumideAbbVieApprovedCFTRCAR-T CD19
SNY-9600SanofiNDA/BLAB7-H3PD-L1i
SNY-8628SanofiNDA/BLAB7-H3TYK2i
SNY-9073SanofiPhase 2B7-H3RAS(ON)i
NVO-7840Novo NordiskPhase 2/3B7-H3GLP-1ag
NVO-7872Novo NordiskNDA/BLAB7-H3BTKi
DSN-5254Daiichi SankyoPhase 1B7-H3ALKi