Modality
Cell Therapy
MOA
USP1i
Target
MDM2
Pathway
Proteasome
PompeADPKD
Development Pipeline
Preclinical
~Jul 2016
→ ~Oct 2017
Phase 1
~Jan 2018
→ ~Apr 2019
Phase 2
~Jul 2019
→ ~Oct 2020
Phase 3
~Jan 2021
→ ~Apr 2022
NDA/BLA
Jul 2022
→ Nov 2031
NDA/BLACurrent
NCT06963354
518 pts·Pompe
2022-07→2031-11·Recruiting
518 total pts1 indication
Approved
CompletedCurrentUpcoming
Catalysts (1)
2031-11-155.6y awayPh3 Readout· Pompe
Trial Timeline
Q3Q42023Q2Q3Q42024Q2Q3Q42025Q2Q3Q42026Q2Q3Q42027Q2Q3Q42028Q2Q3Q42029Q2Q3Q42030Q2Q3Q42031Q2Q3Q4
NDA/BLA
Recruit…
Catalysts
Ph3 Readout
2031-11-15 · 5.6y away
Pompe
Recruiting|StartCompletionToday
Trials (1)
| NCT | Phase | Indication | Status | N | EP |
|---|---|---|---|---|---|
| NCT06963354 | NDA/BLA | Pompe | Recruiting | 518 | HAM-D |
Competitors (10)