← Pipeline|ALN-3958

ALN-3958

Phase 2
Source: Trial-derived·Trials: 1
Modality
Bispecific Ab
MOA
PARPi
Target
MALT1
Pathway
mTOR
PNH
Development Pipeline
Preclinical
~Sep 2020
~Dec 2021
Phase 1
~Mar 2022
~Jun 2023
Phase 2
Sep 2023
Sep 2030
Phase 2Current
NCT07857720
1,046 pts·PNH
2023-092030-09·Not yet recruiting
1,046 total pts1 indication
Phase 3
NDA/BLA
Approved
CompletedCurrentUpcoming
Catalysts (1)
2030-09-274.5y awayPh2 Data· PNH
Trial Timeline
Q42024Q2Q3Q42025Q2Q3Q42026Q2Q3Q42027Q2Q3Q42028Q2Q3Q42029Q2Q3Q42030Q2Q3Q4
P2
Not yet…
Catalysts
Ph2 Data
2030-09-27 · 4.5y away
PNH
Not yet recruiting|StartCompletionToday
Trials (1)
NCTPhaseIndicationStatusNEP
NCT07857720Phase 2PNHNot yet recr...1046ORR
Competitors (10)
DrugCompanyPhaseTargetMOA
JNJ-8232Johnson & JohnsonNDA/BLAMALT1SGLT2i
MRK-3732Merck & CoPhase 1TYK2PARPi
BMY-7975Bristol-Myers SquibbPhase 1MALT1WRNi
GSK-6516GSKPhase 1/2MALT1PARPi
BAY-3684BayerApprovedPD-L1PARPi
BNT-5232BioNTechNDA/BLATIGITPARPi
BII-5240BiogenPhase 2/3MALT1HPK1i
CevisacituzumabAlnylamPreclinicalMALT1SOS1i
CevifotisoranNeurocrineApprovedCD47PARPi
LEG-6533Legend BiotechNDA/BLAVEGFPARPi