← Pipeline|Peminesiran

Peminesiran

Phase 1
ONC-5204
Source: Trial-derived·Trials: 2
Modality
ERT
MOA
KRASG12Ci
Target
TIGIT
Pathway
NF-κB
EpilepsyObesity
Development Pipeline
Preclinical
~Sep 2017
~Dec 2018
Phase 1
Mar 2019
Jun 2026
Phase 1Current
NCT06422837
1,270 pts·Obesity
2019-032025-09·Recruiting
NCT07029718
1,895 pts·Obesity
2020-052026-06·Active
3,165 total pts1 indication
Phase 2
Phase 3
NDA/BLA
Approved
CompletedCurrentUpcoming
Catalysts (3)
2025-08-028mo agoPDUFA· Obesity
2025-09-057mo agoInterim· Obesity
2026-06-213mo awayInterim· Obesity
Trial Timeline
Q2Q3Q42020Q2Q3Q42021Q2Q3Q42022Q2Q3Q42023Q2Q3Q42024Q2Q3Q42025Q2Q3Q42026Q2Q3
P1
Recruit…
P1
Active
Catalysts
PDUFA
2025-08-02 · 8mo ago
Obesity
Interim
2025-09-05 · 7mo ago
Obesity
Interim
2026-06-21 · 3mo away
Obesity
RecruitingActive|StartCompletionToday
Trials (2)
NCTPhaseIndicationStatusNEP
NCT06422837Phase 1ObesityRecruiting1270PFS
NCT07029718Phase 1ObesityActive1895eGFR
Competitors (10)
DrugCompanyPhaseTargetMOA
ZanuderotideJohnson & JohnsonPhase 2/3TIGITGLP-1/GIP
LisolucimabNovartisApprovedCD20KRASG12Ci
GozelemzoparlimabMerck & CoPhase 2FXIaKRASG12Ci
MRK-6781Merck & CoApprovedTIGITRAS(ON)i
AZN-8478AstraZenecaNDA/BLASHP2KRASG12Ci
PexazasiranSanofiPreclinicalFXIaKRASG12Ci
TerasacituzumabNovo NordiskNDA/BLAIL-23KRASG12Ci
PexamavacamtenDaiichi SankyoNDA/BLATIGITCD3xCD20
BNT-5232BioNTechNDA/BLATIGITPARPi
ALN-8757AlnylamPreclinicalTIGITCFTRmod