← Pipeline|Gelizasiran

Gelizasiran

Phase 3
NOR-2017
Source: Trial-derived·Trials: 3
Modality
mAb
MOA
TROP-2 ADC
Target
RET
Pathway
Amyloid
SMABladder CaMigraine
Development Pipeline
Preclinical
~May 2013
~Aug 2014
Phase 1
~Nov 2014
~Feb 2016
Phase 2
~May 2016
~Aug 2017
Phase 3
Nov 2017
Mar 2031
Phase 3Current
NCT07331391
1,648 pts·Migraine
2017-112030-11·Completed
NCT04200084
2,626 pts·Bladder Ca
2019-082031-03·Recruiting
NCT05123011
1,887 pts·Migraine
2025-082026-03·Active
6,161 total pts2 indications
NDA/BLA
Approved
CompletedCurrentUpcoming
Catalysts (3)
2026-03-231w agoPh3 Readout· Migraine
2030-11-244.7y awayPh3 Readout· Migraine
2031-03-124.9y awayPh3 Readout· Bladder Ca
Trial Timeline
Q42018Q2Q3Q42019Q2Q3Q42020Q2Q3Q42021Q2Q3Q42022Q2Q3Q42023Q2Q3Q42024Q2Q3Q42025Q2Q3Q42026Q2Q3Q42027Q2Q3Q42028Q2Q3Q42029Q2Q3Q42030Q2Q3Q42031Q2
P3
Complet…
P3
Recruit…
P3
Active
Catalysts
Ph3 Readout
2026-03-23 · 1w ago
Migraine
Ph3 Readout
2030-11-24 · 4.7y away
Migraine
Ph3 Readout
2031-03-12 · 4.9y away
Bladder Ca
RecruitingActiveCompleted|StartCompletionToday
Trials (3)
NCTPhaseIndicationStatusNEP
NCT07331391Phase 3MigraineCompleted1648LiverFat
NCT04200084Phase 3Bladder CaRecruiting2626BodyWt
NCT05123011Phase 3MigraineActive1887DAS28
Competitors (10)
DrugCompanyPhaseTargetMOA
RHH-5389RochePreclinicalRETSTINGag
FixanesiranAbbViePreclinicalRETJAK1/2i
BMY-8678Bristol-Myers SquibbApprovedRETMDM2i
BAY-6520BayerPhase 2AHRTROP-2 ADC
BemazumabRegeneronPhase 1VEGFTROP-2 ADC
VRT-1576Vertex PharmaPhase 2/3RETSHP2i
ARG-3458ArgenxPreclinicalRETIL-17i
GMA-5010GenmabPhase 3JAK2TROP-2 ADC
INC-1582IncytePhase 1/2APOC3TROP-2 ADC
NidaratamabKrystal BiotechPreclinicalRETIL-17i