← Pipeline|ATH-6254

ATH-6254

Approved
Source: Trial-derived·Trials: 4
Modality
siRNA
MOA
EZH2i
Target
FGFR
Pathway
T-cell
PsA
Development Pipeline
Preclinical
~Sep 2009
~Dec 2010
Phase 1
~Mar 2011
~Jun 2012
Phase 2
~Sep 2012
~Dec 2013
Phase 3
~Mar 2014
~Jun 2015
NDA/BLA
~Sep 2015
~Dec 2016
Approved
Mar 2017
Dec 2031
ApprovedCurrent
NCT08878966
1,944 pts·PsA
2019-112031-12·Terminated
NCT03423876
1,829 pts·PsA
2017-032026-11·Not yet recruiting
NCT03706285
393 pts·PsA
2021-012031-04·Not yet recruiting
+1 more trial
6,110 total pts1 indication
CompletedCurrentUpcoming
Catalysts (4)
2026-11-057mo awayPh3 Readout· PsA
2030-08-264.4y awayPh3 Readout· PsA
2031-04-285.1y awayPh3 Readout· PsA
2031-12-115.7y awayPh3 Readout· PsA
Trial Timeline
2017Q2Q3Q42018Q2Q3Q42019Q2Q3Q42020Q2Q3Q42021Q2Q3Q42022Q2Q3Q42023Q2Q3Q42024Q2Q3Q42025Q2Q3Q42026Q2Q3Q42027Q2Q3Q42028Q2Q3Q42029Q2Q3Q42030Q2Q3Q42031Q2Q3Q4
Approved
Not yet…
Approved
Termina…
Approved
Not yet…
Approved
Not yet…
Catalysts
Ph3 Readout
2026-11-05 · 7mo away
PsA
Ph3 Readout
2030-08-26 · 4.4y away
PsA
Ph3 Readout
2031-04-28 · 5.1y away
PsA
Ph3 Readout
2031-12-11 · 5.7y away
PsA
TerminatedNot yet recruiting|StartCompletionToday
Trials (4)
NCTPhaseIndicationStatusNEP
NCT08878966ApprovedPsATerminated1944Safety
NCT03423876ApprovedPsANot yet recr...1829CR
NCT03706285ApprovedPsANot yet recr...393MRD
NCT03778520ApprovedPsANot yet recr...1944Biomarker
Competitors (10)
DrugCompanyPhaseTargetMOA
LLY-1592Eli LillyNDA/BLAFGFRBETi
AdagrazumabNovartisPhase 2/3Cl18.2EZH2i
DoxarasimodMerck & CoNDA/BLAFGFRKRASG12Di
RibotuximabMerck & CoPhase 2GPRC5DEZH2i
AZN-7403AstraZenecaPhase 2/3FGFRTNFi
NVO-9615Novo NordiskPhase 2/3PRMT5EZH2i
CevitinibRegeneronPhase 3FGFRPCSK9i
PolalucimabJazz PharmaPreclinicalPLK4EZH2i
ASN-7038Ascendis PharmaPhase 3VEGFEZH2i
LiratinibKrystal BiotechNDA/BLATIM-3EZH2i