← Pipeline|Gozenesiran

Gozenesiran

NDA/BLA
ALG-2193
Source: Trial-derived·Trials: 2
Modality
Nanobody
MOA
GLP-1/GIP
Target
CD20
Pathway
Ferroptosis
MG
Development Pipeline
Preclinical
~Aug 2012
~Nov 2013
Phase 1
~Feb 2014
~May 2015
Phase 2
~Aug 2015
~Nov 2016
Phase 3
~Feb 2017
~May 2018
NDA/BLA
Aug 2018
Nov 2027
NDA/BLACurrent
NCT03991234
1,304 pts·MG
2025-072027-11·Terminated
NCT06577846
2,074 pts·MG
2018-08TBD·Completed
3,378 total pts1 indication
Approved
CompletedCurrentUpcoming
Catalysts (1)
2027-11-271.7y awayPh3 Readout· MG
Trial Timeline
Q3Q42019Q2Q3Q42020Q2Q3Q42021Q2Q3Q42022Q2Q3Q42023Q2Q3Q42024Q2Q3Q42025Q2Q3Q42026Q2Q3Q42027Q2Q3Q4
NDA/BLA
Complet…
NDA/BLA
Termina…
Catalysts
Ph3 Readout
2027-11-27 · 1.7y away
MG
CompletedTerminated|StartCompletionToday
Trials (2)
NCTPhaseIndicationStatusNEP
NCT03991234NDA/BLAMGTerminated1304SRI-4
NCT06577846NDA/BLAMGCompleted2074LiverFat
Competitors (10)
DrugCompanyPhaseTargetMOA
ZanuderotideJohnson & JohnsonPhase 2/3TIGITGLP-1/GIP
JNJ-8168Johnson & JohnsonPhase 2/3FLT3GLP-1/GIP
JNJ-8637Johnson & JohnsonNDA/BLACD20WEE1i
LisolucimabNovartisApprovedCD20KRASG12Ci
ABB-8985AbbViePhase 2CD20MALT1i
AZN-5171AstraZenecaApprovedGLP-1RGLP-1/GIP
ARG-3265ArgenxPhase 1/2CD20CDK2i
PemiinavolisibSareptaNDA/BLACD47GLP-1/GIP
CRS-6525CRISPR TherapeuticsPhase 2CD20HPK1i
BEA-4274BeamPhase 1/2ALKGLP-1/GIP