← Pipeline|Nidanesiran

Nidanesiran

Approved
GEN-7410
Source: Trial-derived·Trials: 4
Modality
siRNA
MOA
IL-13i
Target
CDK4/6
Pathway
Incretin
RA
Development Pipeline
Preclinical
~Feb 2011
~May 2012
Phase 1
~Aug 2012
~Nov 2013
Phase 2
~Feb 2014
~May 2015
Phase 3
~Aug 2015
~Nov 2016
NDA/BLA
~Feb 2017
~May 2018
Approved
Aug 2018
Oct 2031
ApprovedCurrent
NCT06709725
1,398 pts·RA
2023-102031-10·Recruiting
NCT04447027
1,476 pts·RA
2020-052028-03·Completed
NCT08473105
1,258 pts·RA
2018-082025-05·Terminated
+1 more trial
6,857 total pts1 indication
CompletedCurrentUpcoming
Catalysts (4)
2025-05-2210mo agoPh3 Readout· RA
2028-03-232.0y awayPh3 Readout· RA
2029-12-123.7y awayPh3 Readout· RA
2031-10-255.6y awayPh3 Readout· RA
Trial Timeline
Q3Q42019Q2Q3Q42020Q2Q3Q42021Q2Q3Q42022Q2Q3Q42023Q2Q3Q42024Q2Q3Q42025Q2Q3Q42026Q2Q3Q42027Q2Q3Q42028Q2Q3Q42029Q2Q3Q42030Q2Q3Q42031Q2Q3Q4
Approved
Termina…
Approved
Complet…
Approved
Not yet…
Approved
Recruit…
Catalysts
Ph3 Readout
2025-05-22 · 10mo ago
RA
Ph3 Readout
2028-03-23 · 2.0y away
RA
Ph3 Readout
2029-12-12 · 3.7y away
RA
Ph3 Readout
2031-10-25 · 5.6y away
RA
RecruitingCompletedTerminatedNot yet recruiting|StartCompletionToday
Trials (4)
NCTPhaseIndicationStatusNEP
NCT06709725ApprovedRARecruiting1398Mayo
NCT04447027ApprovedRACompleted1476VA
NCT08473105ApprovedRATerminated1258LiverFat
NCT03299431ApprovedRANot yet recr...2725EDSS
Competitors (10)
DrugCompanyPhaseTargetMOA
VoxaderotideJohnson & JohnsonNDA/BLAPI3KαIL-13i
RHH-7975RochePhase 3FXIaIL-13i
NVS-8902NovartisPreclinicalTROP-2IL-13i
GozesotorasibBristol-Myers SquibbNDA/BLAHER2IL-13i
BMY-4586Bristol-Myers SquibbPreclinicalKRASG12CIL-13i
AMG-1919AmgenPhase 2/3CDK2IL-13i
MotavorutinibAmgenPhase 3CDK4/6JAK1/2i
RibozanubrutinibRegeneronPhase 1CDK4/6IL-13i
MRN-5715ModernaNDA/BLACDK4/6AuroraAi
ROI-3353Roivant SciencesPhase 1/2PLK4IL-13i