← Pipeline|Mirimavacamten

Mirimavacamten

Phase 1
TXG-9552
Source: Trial-derived·Trials: 1
Modality
ASO
MOA
ALKi
Target
PSMA
Pathway
Epigenetic
Myelofibrosis
Development Pipeline
Preclinical
~Jun 2018
~Sep 2019
Phase 1
Dec 2019
Phase 1Current
NCT03571847
1,376 pts·Myelofibrosis
2019-12TBD·Recruiting
1,376 total pts1 indication
Phase 2
Phase 3
NDA/BLA
Approved
CompletedCurrentUpcoming
Trial Timeline
P1
Recruit…
Recruiting|StartCompletionToday
Trials (1)
NCTPhaseIndicationStatusNEP
NCT03571847Phase 1MyelofibrosisRecruiting1376PASI75
Competitors (10)
DrugCompanyPhaseTargetMOA
MiriosocimabPfizerPhase 1PARPALKi
MRK-7739Merck & CoPreclinicalIL-23ALKi
AZN-3724AstraZenecaPreclinicalPSMABCMA ADC
BMY-2495Bristol-Myers SquibbPhase 3KRASG12DALKi
DoxacageneSanofiApprovedPSMASHP2i
GSK-2051GSKPhase 1PSMAEGFRi
DSN-5254Daiichi SankyoPhase 1B7-H3ALKi
SovacapivasertibAmgenPhase 3WEE1ALKi
ZanuratamabGilead SciencesPhase 1/2CDK2ALKi
GIL-2445Gilead SciencesPhase 2/3PSMAALKi