Modality
Small Molecule
MOA
EGFRi
Target
AuroraA
Pathway
Wnt
Hemophilia A
Development Pipeline
Preclinical
~Jul 2019
→ ~Oct 2020
Phase 1
~Jan 2021
→ ~Apr 2022
Phase 2
~Jul 2022
→ ~Oct 2023
Phase 3
Jan 2024
Phase 3Current
NCT07860186
397 pts·Hemophilia A
2024-01→TBD·Active
397 total pts1 indication
NDA/BLA
Approved
CompletedCurrentUpcoming
Catalysts (1)
2025-11-115mo agoConference· Hemophilia A
Trial Timeline
2024Q2Q3Q42025Q2Q3Q4
P3
Active
Catalysts
Conference
2025-11-11 · 5mo ago
Hemophilia A
Active|StartCompletionToday
Trials (1)
| NCT | Phase | Indication | Status | N | EP |
|---|---|---|---|---|---|
| NCT07860186 | Phase 3 | Hemophilia A | Active | 397 | SeizFreq |
Competitors (10)
| Drug | Company | Phase | Target | MOA |
|---|---|---|---|---|
| Niranesiran | Johnson & Johnson | Phase 2 | KIF18A | |
| JNJ-5094 | Johnson & Johnson | Phase 2/3 | GIP-R | |
| Motarapivir | GSK | Preclinical | AuroraA | |
| GSK-2051 | GSK | Phase 1 | PSMA | |
| BAY-8733 | Bayer | Preclinical | AuroraA | |
| GIL-8529 | Gilead Sciences | Phase 1/2 | JAK1 | |
| BNT-8090 | BioNTech | Phase 2 | AuroraA | |
| ARG-6988 | Argenx | Preclinical | AuroraA | |
| 207-2754 | Samsung Biologics | Phase 1/2 | KRASG12D | |
| Mavuratamab | Blueprint Medicines | NDA/BLA | BET |