← Pipeline|Pemizasiran

Pemizasiran

NDA/BLA
WIN-1835
Source: Trial-derived·Trials: 2
Modality
ASO
MOA
WEE1i
Target
GLP-1R
Pathway
PD-1/PD-L1
GBM
Development Pipeline
Preclinical
~Aug 2011
~Nov 2012
Phase 1
~Feb 2013
~May 2014
Phase 2
~Aug 2014
~Nov 2015
Phase 3
~Feb 2016
~May 2017
NDA/BLA
Aug 2017
Aug 2031
NDA/BLACurrent
NCT04316589
2,847 pts·GBM
2017-082030-03·Terminated
NCT07364360
2,042 pts·GBM
2024-062031-08·Recruiting
4,889 total pts1 indication
Approved
CompletedCurrentUpcoming
Catalysts (2)
2030-03-254.0y awayPh3 Readout· GBM
2031-08-225.4y awayPh3 Readout· GBM
Trial Timeline
Q3Q42018Q2Q3Q42019Q2Q3Q42020Q2Q3Q42021Q2Q3Q42022Q2Q3Q42023Q2Q3Q42024Q2Q3Q42025Q2Q3Q42026Q2Q3Q42027Q2Q3Q42028Q2Q3Q42029Q2Q3Q42030Q2Q3Q42031Q2Q3Q4
NDA/BLA
Termina…
NDA/BLA
Recruit…
Catalysts
Ph3 Readout
2030-03-25 · 4.0y away
GBM
Ph3 Readout
2031-08-22 · 5.4y away
GBM
RecruitingTerminated|StartCompletionToday
Trials (2)
NCTPhaseIndicationStatusNEP
NCT04316589NDA/BLAGBMTerminated2847HAM-D
NCT07364360NDA/BLAGBMRecruiting2042PANSS
Competitors (10)
DrugCompanyPhaseTargetMOA
PFE-2191PfizerNDA/BLAGLP-1RSHP2i
JNJ-8637Johnson & JohnsonNDA/BLACD20WEE1i
RiboinavolisibJohnson & JohnsonPhase 2/3GLP-1RMALT1i
TirzepatideEli LillyApprovedGLP-1RGLP-1/GIP Dual Agonist
MRK-853Merck & CoPhase 1PRMT5WEE1i
MRK-5413Merck & CoPhase 1GLP-1RVEGFi
VoxacilimabAstraZenecaPhase 1/2GLP-1RPI3Ki
AZN-5171AstraZenecaApprovedGLP-1RGLP-1/GIP
MavuglumideBayerApprovedGLP-1RCDK2i
DoxafotisoranDaiichi SankyoPhase 1Cl18.2WEE1i