← Pipeline|Fixazasiran

Fixazasiran

Approved
226-9000
Source: Trial-derived·Trials: 4
Modality
Peptide
MOA
Cl18.2
Target
MDM2
Pathway
RAS/MAPK
Thymoma
Development Pipeline
Preclinical
~Sep 2011
~Dec 2012
Phase 1
~Mar 2013
~Jun 2014
Phase 2
~Sep 2014
~Dec 2015
Phase 3
~Mar 2016
~Jun 2017
NDA/BLA
~Sep 2017
~Dec 2018
Approved
Mar 2019
May 2030
ApprovedCurrent
NCT03346172
678 pts·Thymoma
2022-092030-05·Not yet recruiting
NCT05998123
32 pts·Thymoma
2021-062030-02·Active
NCT04095674
2,583 pts·Thymoma
2022-072028-03·Not yet recruiting
+1 more trial
5,765 total pts1 indication
CompletedCurrentUpcoming
Catalysts (4)
2025-05-2010mo agoPh3 Readout· Thymoma
2028-03-091.9y awayPh3 Readout· Thymoma
2030-02-203.9y awayPh3 Readout· Thymoma
2030-05-184.1y awayPh3 Readout· Thymoma
Trial Timeline
2019Q2Q3Q42020Q2Q3Q42021Q2Q3Q42022Q2Q3Q42023Q2Q3Q42024Q2Q3Q42025Q2Q3Q42026Q2Q3Q42027Q2Q3Q42028Q2Q3Q42029Q2Q3Q42030Q2Q3
Approved
Complet…
Approved
Active
Approved
Not yet…
Approved
Not yet…
Catalysts
Ph3 Readout
2025-05-20 · 10mo ago
Thymoma
Ph3 Readout
2028-03-09 · 1.9y away
Thymoma
Ph3 Readout
2030-02-20 · 3.9y away
Thymoma
Ph3 Readout
2030-05-18 · 4.1y away
Thymoma
ActiveCompletedNot yet recruiting|StartCompletionToday
Trials (4)
NCTPhaseIndicationStatusNEP
NCT03346172ApprovedThymomaNot yet recr...678PASI75
NCT05998123ApprovedThymomaActive32DOR
NCT04095674ApprovedThymomaNot yet recr...2583CR
NCT04012603ApprovedThymomaCompleted2472EDSS
Competitors (10)
DrugCompanyPhaseTargetMOA
LLY-6079Eli LillyPhase 2MDM2PRMT5i
LLY-3251Eli LillyPhase 2MDM2BiTE
ZorivorutinibBristol-Myers SquibbApprovedDLL3Cl18.2
GSK-7987GSKPhase 3MDM2PD-1i
AMG-2752AmgenPreclinicalMDM2WRNi
REG-3155RegeneronPhase 1/2MDM2PI3Ki
ElrarapivirRegeneronPhase 1GIP-RCl18.2
SRP-1135SareptaPhase 2/3MDM2PD-L1i
HAL-9635HalozymePhase 2/3EZH2Cl18.2
VKT-6548Viking TherapeuticsPhase 2/3PD-L1Cl18.2