← Pipeline|Pexafotisoran

Pexafotisoran

Phase 1/2
AIM-5409
Source: Trial-derived·Trials: 2
Modality
Small Molecule
MOA
C5i
Target
GIP-R
Pathway
JAK/STAT
Parkinson's
Development Pipeline
Preclinical
~Nov 2019
~Feb 2021
Phase 1
May 2021
Sep 2028
Phase 1Current
NCT06468830
146 pts·Parkinson's
2021-052028-09·Not yet recruiting
NCT07333612
2,718 pts·Parkinson's
2021-072025-11·Recruiting
2,864 total pts1 indication
Phase 2
Phase 3
NDA/BLA
Approved
CompletedCurrentUpcoming
Catalysts (2)
2025-11-284mo agoPh2 Data· Parkinson's
2028-09-222.5y awayPh2 Data· Parkinson's
Trial Timeline
Q2Q3Q42022Q2Q3Q42023Q2Q3Q42024Q2Q3Q42025Q2Q3Q42026Q2Q3Q42027Q2Q3Q42028Q2Q3Q4
P1/2
Not yet…
P1/2
Recruit…
Catalysts
Ph2 Data
2025-11-28 · 4mo ago
Parkinson's
Ph2 Data
2028-09-22 · 2.5y away
Parkinson's
RecruitingNot yet recruiting|StartCompletionToday
Trials (2)
NCTPhaseIndicationStatusNEP
NCT06468830Phase 1/2Parkinson'sNot yet recr...146BodyWt
NCT07333612Phase 1/2Parkinson'sRecruiting2718HAM-D
Competitors (10)
DrugCompanyPhaseTargetMOA
JNJ-5094Johnson & JohnsonPhase 2/3GIP-REGFRi
RHH-3592RochePhase 1/2GIP-RBCL-2i
AZN-5978AstraZenecaPhase 2/3GIP-RAHRant
IvotuximabGSKNDA/BLAGIP-RKRASG12Di
DSN-2247Daiichi SankyoNDA/BLAEZH2C5i
ElrarapivirRegeneronPhase 1GIP-RCl18.2
CapifutibatinibIntra-CellularPhase 3GIP-RVEGFi
RimabrutinibMadrigal PharmaPhase 1/2GPRC5DC5i
XEN-577Xenon PharmaPhase 2/3C5C5i
TNG-8610Tango TherNDA/BLAGIP-RAnti-Aβ