← Pipeline|Ribonesiran

Ribonesiran

Phase 1/2
451-7780
Source: Trial-derived·Trials: 2
Modality
Gene Therapy
MOA
SOS1i
Target
IL-23
Pathway
Neuroinflam
MDDGastric Ca
Development Pipeline
Preclinical
~May 2019
~Aug 2020
Phase 1
Nov 2020
Apr 2031
Phase 1Current
NCT04600093
2,155 pts·MDD
2020-112025-01·Recruiting
NCT07649708
516 pts·Gastric Ca
2023-092031-04·Not yet recruiting
2,671 total pts2 indications
Phase 2
Phase 3
NDA/BLA
Approved
CompletedCurrentUpcoming
Catalysts (2)
2025-01-261.2y agoPh2 Data· MDD
2031-04-215.1y awayPh2 Data· Gastric Ca
Trial Timeline
Q42021Q2Q3Q42022Q2Q3Q42023Q2Q3Q42024Q2Q3Q42025Q2Q3Q42026Q2Q3Q42027Q2Q3Q42028Q2Q3Q42029Q2Q3Q42030Q2Q3Q42031Q2Q3
P1/2
Recruit…
P1/2
Not yet…
Catalysts
Ph2 Data
2025-01-26 · 1.2y ago
MDD
Ph2 Data
2031-04-21 · 5.1y away
Gastric Ca
RecruitingNot yet recruiting|StartCompletionToday
Trials (2)
NCTPhaseIndicationStatusNEP
NCT04600093Phase 1/2MDDRecruiting2155OS
NCT07649708Phase 1/2Gastric CaNot yet recr...516Mayo
Competitors (10)
DrugCompanyPhaseTargetMOA
PFE-2901PfizerPhase 2AHRSOS1i
MRK-7739Merck & CoPreclinicalIL-23ALKi
MRK-1380Merck & CoPreclinicalSHP2SOS1i
TerarelsinAbbViePreclinicalSOS1SOS1i
DoxarapivirBristol-Myers SquibbPhase 3KRASG12CSOS1i
TerasacituzumabNovo NordiskNDA/BLAIL-23KRASG12Ci
DSN-6862Daiichi SankyoPreclinicalIL-23SOS1i
GIL-2011Gilead SciencesPreclinicalVEGFSOS1i
REG-647RegeneronPreclinicalSMN2SOS1i
TezecilimabRegeneronApprovedIL-23CGRPant