← Pipeline|Lisomavacamten

Lisomavacamten

NDA/BLA
153-5271
Source: Trial-derived·Trials: 2
Modality
Nanobody
MOA
HER2
Target
IL-17A
Pathway
Notch
CF
Development Pipeline
Preclinical
~May 2014
~Aug 2015
Phase 1
~Nov 2015
~Feb 2017
Phase 2
~May 2017
~Aug 2018
Phase 3
~Nov 2018
~Feb 2020
NDA/BLA
May 2020
Mar 2027
NDA/BLACurrent
NCT07519913
2,239 pts·CF
2021-092026-08·Completed
NCT08743710
643 pts·CF
2020-052027-03·Not yet recruiting
2,882 total pts1 indication
Approved
CompletedCurrentUpcoming
Catalysts (2)
2026-08-114mo awayPh3 Readout· CF
2027-03-1211mo awayPh3 Readout· CF
Trial Timeline
Q2Q3Q42021Q2Q3Q42022Q2Q3Q42023Q2Q3Q42024Q2Q3Q42025Q2Q3Q42026Q2Q3Q42027Q2
NDA/BLA
Not yet…
NDA/BLA
Complet…
Catalysts
Ph3 Readout
2026-08-11 · 4mo away
CF
Ph3 Readout
2027-03-12 · 11mo away
CF
CompletedNot yet recruiting|StartCompletionToday
Trials (2)
NCTPhaseIndicationStatusNEP
NCT07519913NDA/BLACFCompleted2239OS
NCT08743710NDA/BLACFNot yet recr...643VA
Competitors (10)
DrugCompanyPhaseTargetMOA
PFE-7809PfizerPhase 1DLL3HER2
LLY-8903Eli LillyPreclinicalCD47HER2
GeliderotideNovartisNDA/BLAIL-17ABCL-2i
SNY-7254SanofiPhase 2CFTRHER2
DatobrutinibSanofiPhase 3HER2
TAK-9344TakedaPhase 3CGRPHER2
TirasotorasibTakedaNDA/BLAIL-17ACDK2i
GIL-9779Gilead SciencesPhase 1IL-17ABCMA ADC
RVM-7089Revolution MedicinesPhase 3IL-17AMALT1i
VoxaderotideViking TherapeuticsApprovedPD-L1HER2