← Pipeline|Mavumavacamten

Mavumavacamten

Phase 3
KLB-8056
Source: Trial-derived·Trials: 3
Modality
Radioligand
MOA
Menini
Target
DLL3
Pathway
Proteasome
MDS
Development Pipeline
Preclinical
~Dec 2015
~Mar 2017
Phase 1
~Jun 2017
~Sep 2018
Phase 2
~Dec 2018
~Mar 2020
Phase 3
Jun 2020
Feb 2026
Phase 3Current
NCT04524918
2,794 pts·MDS
2020-062025-08·Not yet recruiting
NCT07325513
1,466 pts·MDS
2021-062026-02·Recruiting
NCT05500973
1,231 pts·MDS
2020-07TBD·Completed
5,491 total pts1 indication
NDA/BLA
Approved
CompletedCurrentUpcoming
Catalysts (2)
2025-08-257mo agoPh3 Readout· MDS
2026-02-151mo agoPh3 Readout· MDS
Trial Timeline
Q3Q42021Q2Q3Q42022Q2Q3Q42023Q2Q3Q42024Q2Q3Q42025Q2Q3Q42026
P3
Not yet…
P3
Complet…
P3
Recruit…
Catalysts
Ph3 Readout
2025-08-25 · 7mo ago
MDS
Ph3 Readout
2026-02-15 · 1mo ago
MDS
RecruitingCompletedNot yet recruiting|StartCompletionToday
Trials (3)
NCTPhaseIndicationStatusNEP
NCT04524918Phase 3MDSNot yet recr...2794EFS
NCT07325513Phase 3MDSRecruiting1466Biomarker
NCT05500973Phase 3MDSCompleted1231LiverFat
Competitors (10)
DrugCompanyPhaseTargetMOA
PFE-7809PfizerPhase 1DLL3HER2
MavutenlimabJohnson & JohnsonPhase 3Cl18.2Menini
IvorelsinEli LillyApprovedJAK1Menini
PexarelsinAstraZenecaPhase 1DLL3KRASG12Di
ZorivorutinibBristol-Myers SquibbApprovedDLL3Cl18.2
NVO-2974Novo NordiskNDA/BLAPARPMenini
ZenonesiranGSKPreclinicalDLL3CD47i
AMG-7379AmgenPreclinicalDLL3CD47i
ARG-1924ArgenxPreclinicalDLL3JAK1i
CevinaritideGenmabPhase 2/3DLL3PD-1i