← Pipeline|Mirinesiran

Mirinesiran

Phase 2
NOI-5293
Source: Trial-derived·Trials: 2
Modality
Degrader
MOA
EGFRi
Target
FcRn
Pathway
PI3K/AKT
CeliacFTDCRC
Development Pipeline
Preclinical
~Mar 2014
~Jun 2015
Phase 1
~Sep 2015
~Dec 2016
Phase 2
Mar 2017
Feb 2025
Phase 2Current
NCT05509066
565 pts·Celiac
2020-062025-02·Completed
NCT04345307
1,525 pts·FTD
2017-03TBD·Active
2,090 total pts2 indications
Phase 3
NDA/BLA
Approved
CompletedCurrentUpcoming
Catalysts (1)
2025-02-141.1y agoPh2 Data· Celiac
Trial Timeline
Q2Q3Q42018Q2Q3Q42019Q2Q3Q42020Q2Q3Q42021Q2Q3Q42022Q2Q3Q42023Q2Q3Q42024Q2Q3Q42025Q2
P2
Active
P2
Complet…
Catalysts
Ph2 Data
2025-02-14 · 1.1y ago
Celiac
ActiveCompleted|StartCompletionToday
Trials (2)
NCTPhaseIndicationStatusNEP
NCT05509066Phase 2CeliacCompleted565DAS28
NCT04345307Phase 2FTDActive15256MWD
Competitors (10)
DrugCompanyPhaseTargetMOA
NiranesiranJohnson & JohnsonPhase 2KIF18AEGFRi
JNJ-5094Johnson & JohnsonPhase 2/3GIP-REGFRi
CevizanubrutinibJohnson & JohnsonPreclinicalFcRnCD47i
GelinaritideAbbViePreclinicalFcRnCFTRmod
GSK-2051GSKPhase 1PSMAEGFRi
TalalemzoparlimabGilead SciencesPhase 1FcRnTNFi
GIL-8529Gilead SciencesPhase 1/2JAK1EGFRi
SovafutibatinibModernaApprovedFcRnSHP2i
ITC-879Intra-CellularApprovedFcRnTYK2i
JAZ-8729Jazz PharmaPhase 2/3FcRnCAR-T BCMA