Modality
Fusion Protein
MOA
RAS(ON)i
Target
USP1
Pathway
RNA Splicing
RCCLNAML
Development Pipeline
Preclinical
~Jun 2022
→ ~Sep 2023
Phase 1
~Dec 2023
→ ~Mar 2025
Phase 2
Jun 2025
→ Jan 2031
Phase 2Current
NCT07235669
1,779 pts·AML
2025-06→2031-01·Recruiting
1,779 total pts1 indication
Phase 3
NDA/BLA
Approved
CompletedCurrentUpcoming
Catalysts (1)
2031-01-044.8y awayPh2 Data· AML
Trial Timeline
Q3Q42026Q2Q3Q42027Q2Q3Q42028Q2Q3Q42029Q2Q3Q42030Q2Q3Q42031
P2
Recruit…
Catalysts
Ph2 Data
2031-01-04 · 4.8y away
AML
Recruiting|StartCompletionToday
Trials (1)
| NCT | Phase | Indication | Status | N | EP |
|---|---|---|---|---|---|
| NCT07235669 | Phase 2 | AML | Recruiting | 1779 | ACR20 |
Competitors (10)
| Drug | Company | Phase | Target | MOA |
|---|---|---|---|---|
| MRK-6781 | Merck & Co | Approved | TIGIT | |
| ABB-2476 | AbbVie | Phase 1/2 | USP1 | |
| SNY-9073 | Sanofi | Phase 2 | B7-H3 | |
| Tixarelsin | Vertex Pharma | Phase 1 | ALK | |
| Fixatuximab | Legend Biotech | Preclinical | CFTR | |
| ION-1378 | Ionis | NDA/BLA | TROP-2 | |
| 180-3597 | Innovent Bio | Preclinical | SHP2 | |
| CGO-2579 | CG Oncology | Approved | TIGIT | |
| Tezesotorasib | Enliven | Phase 2 | USP1 | |
| ETN-5063 | 89bio | Phase 1/2 | USP1 |