ADPKD

59 programs · 58 companies

Programs
59
Companies
58
Trials
66
MOAs
36
JAK1/2iEGFRiUSP1iALKiGLP-1agEZH2iBETiSHP2iCDK4/6iBCMA ADC
Drugs
DrugCompanyPhaseTargetMOA
VRT-9481Vertex PharmaPhase 1/2MeninJAK1/2i
BemaderotideRevolution MedicinesPhase 3BCL-2EGFRi
ITO-535iTeosNDA/BLAMDM2USP1i
SLR-5251AcelyrinPhase 3KRASG12DALKi
TalainavolisibFate TherApprovedKIF18AGLP-1ag
PEK-IIT-463Peking Univ Cancer HospPreclinicalWEE1EZH2i
DUK-IIT-841Duke Cancer InstitutePhase 1C5BETi
AVX-9264AnavexPhase 2/3CD20SHP2i
CRV-1020CervoMedApprovedCDK4/6USP1i
TixaglumideCompass TherPreclinicalC5CDK4/6i
LirasacituzumabMBX BioPreclinicalPCSK9BCMA ADC
KAR-4717Kartos TherPreclinicalNectin-4CD3xCD20
ZoritenlimabFlare TherPreclinicalCDK4/6SGLT2i
TeracilimabZevra TherapeuticsPhase 2/3TIGITCAR-T CD19
XBI-1781XBiotechPhase 3WRNFcRni
FixaratamabMiNT TherapeuticsPhase 1/2PD-L1IL-17i
TeralucimabMarker TherapeuticsApprovedSMN2CDK4/6i
IMM-2816Immunomedics (Gilead)ApprovedCl18.2PD-1i
DMA-2916DiaMedica TherapeuticsPhase 1/2CD38Menini
ElrafotisoranPharmaCyte BiotechPhase 3FLT3SGLT2i
PemifutibatinibSecond SightPhase 2/3IL-13WRNi
AdagrainavolisibG1 Therapeutics (Licella)Phase 2/3FcRnSGLT2i
TezezasiranVolato GroupPhase 2PRMT5WRNi
SurazumabIMV (renamed Immunovaccine)PreclinicalFLT3KIF18Ai
GLT-1490GalectoPhase 1Nectin-4HER2
SHI-2989Shire (Takeda)Phase 2AHRSTINGag
ZanufotisoranSynthorx (Sanofi)ApprovedBETTYK2i
NidazumabForty Seven (Gilead)Phase 1/2KRASG12CBCMA ADC
IvozasiranAlteogenPhase 3CFTRBCL-2i
NOR-4666NorthStar MedPhase 3IL-13HER2
AMB-7870Ambys MedPhase 3IL-13KRASG12Di
IMM-5834ImmunaiPhase 2FGFRKIF18Ai
TalazasiranREGENXBIOApprovedPLK4EZH2i
ACL-6459ArcellxPhase 3FGFREZH2i
IvoratamabDesign TherPhase 2/3TauBCL-2i
LisozasiranFulcrum TherNDA/BLAIL-17ABiTE
MirisertibMimetogenPhase 3CD19Anti-Tau
SovazumabAdamas (Supernus)Phase 1IL-13EZH2i
418-6056Mitsubishi TanabePhase 1/2BCL-2GLP-1ag
NidacilimabAurobindoApprovedJAK2CDK2i
NidarelsinAutolus TherApprovedFGFRCAR-T BCMA
MRK-7986Merck KGaAPhase 1/2WRNSHP2i
TirazumabPlurilockPhase 2/3KIF18ASHP2i
TXM-5550TherapeuticsMDNDA/BLAKRASG12CBCL-2i
FixabrutinibPolyphorPhase 1METFXIai
PexasertibNuevolution (Amgen)ApprovedMETJAK1/2i
TerarelsinLaboratorios RoviPhase 1/2TIGITMenini
IvonesiranLaboratorios RoviPhase 1/2CGRPFGFRi
GozesertibMithra PharmaPhase 1/2CDK2JAK1/2i
TalafutibatinibAlkem LabsPhase 3TROP-2IL-23i
SurasertibWockhardtPhase 1/2CGRPPRMT5i
ZYD-981Zydus LifesciencesPreclinicalTIGITCAR-T CD19
BIO-1735Biogenesis BagoPhase 2Cl18.2FXIai
300-8538Zhifei BiologicalNDA/BLAPLK4Cl18.2
RimamavacamtenScientus PharmaPreclinicalGPRC5DSOS1i
RGE-6554RepligenPhase 1SMN2FcRni
WST-3903West PharmaPreclinicalFXIaJAK1/2i
DEC-8558Dechra Pharma (EQT)PreclinicalCl18.2MALT1i
NEO-8617NeogenPhase 1/2CD3IL-13i
Trials (66)
NCTDrugPhaseStatus
NCT08045492VRT-9481Phase 1/2Terminated
NCT04680525SLR-5251Phase 3Terminated
NCT05501447TalainavolisibApprovedRecruiting
NCT07816425TalainavolisibApprovedActive
NCT07555894PEK-IIT-463PreclinicalCompleted
NCT08650235DUK-IIT-841Phase 1Recruiting
NCT08271356TixaglumidePreclinicalActive
NCT07366269KAR-4717PreclinicalActive
NCT05064970KAR-4717PreclinicalCompleted
NCT08250767ZoritenlimabPreclinicalCompleted
NCT04103386XBI-1781Phase 3Terminated
NCT06260699XBI-1781Phase 3Completed
NCT06797973XBI-1781Phase 3Terminated
NCT06163185FixaratamabPhase 1/2Completed
NCT03953076TeralucimabApprovedCompleted
NCT06815771IMM-2816ApprovedCompleted
NCT06450807DMA-2916Phase 1/2Recruiting
NCT05314823DMA-2916Phase 1/2Active
NCT07296031ElrafotisoranPhase 3Active
NCT05745977ElrafotisoranPhase 3Not yet recr...