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REGENXBIO

RGNX·NASDAQRockville MDFounded 2009300 employees
Small CapbiotechPublicOphthalmologyNeurology
Platform: NAV AAV
Market Cap
$0.5B
All Drugs
2
Clinical Trials
3
Failed / Terminated
0
FDA Approved
1
Stock Price & Catalysts (RGNX)
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Drug Pipeline (2 programs)
Drug NameCodePhaseTrialsModalityTargetMOAIndications
RGN-9803RGN-9803NDA/BLA2NanobodyRETC5iSLESCD
TalazasiranRGN-7746Approved1mAbPLK4EZH2iADPKDAS
SEC Filings & Financial Documents
Insider Trading Activity
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Catalyst Events (3)
2026-04-21
RGN-9803 Ph3 Readout
SCD
Ph3 Readout
2027-05-19
Talazasiran Ph3 Readout
ADPKD
Ph3 Readout
2028-02-25
RGN-9803 Ph3 Readout
SLE
Ph3 Readout