← Pipeline|Gozecagene

Gozecagene

Phase 1
BIO-2010
Source: Trial-derived·Trials: 1
Modality
ADC
MOA
BCL-2i
Target
GPRC5D
Pathway
RNA Splicing
NMOSDACCNASH
Development Pipeline
Preclinical
~Nov 2021
~Feb 2023
Phase 1
May 2023
Oct 2031
Phase 1Current
NCT04586726
850 pts·NASH
2023-052031-10·Completed
850 total pts1 indication
Phase 2
Phase 3
NDA/BLA
Approved
CompletedCurrentUpcoming
Catalysts (1)
2031-10-115.5y awayInterim· NASH
Trial Timeline
Q2Q3Q42024Q2Q3Q42025Q2Q3Q42026Q2Q3Q42027Q2Q3Q42028Q2Q3Q42029Q2Q3Q42030Q2Q3Q42031Q2Q3Q4
P1
Complet…
Catalysts
Interim
2031-10-11 · 5.5y away
NASH
Completed|StartCompletionToday
Trials (1)
NCTPhaseIndicationStatusNEP
NCT04586726Phase 1NASHCompleted850SRI-4
Competitors (10)
DrugCompanyPhaseTargetMOA
PFE-5501PfizerPhase 1BTKBCL-2i
RHH-3592RochePhase 1/2GIP-RBCL-2i
PexatenlimabNovartisPhase 1/2GPRC5DKIF18Ai
GeliderotideNovartisNDA/BLAIL-17ABCL-2i
RibotuximabMerck & CoPhase 2GPRC5DEZH2i
BMY-9931Bristol-Myers SquibbPhase 1GPRC5DFXIai
NVO-7877Novo NordiskPreclinicalGPRC5DFXIai
TezecilimabTakedaNDA/BLATauBCL-2i
AMG-9654AmgenPhase 2GPRC5DDLL3 ADC
RimaosocimabAmgenPreclinicalFXIaBCL-2i