← Pipeline|GMA-1468

GMA-1468

NDA/BLA
Source: Trial-derived·Trials: 1
Modality
Peptide
MOA
WEE1i
Target
PI3Kα
Pathway
PD-1/PD-L1
T2DNMOSDLN
Development Pipeline
Preclinical
~Nov 2017
~Feb 2019
Phase 1
~May 2019
~Aug 2020
Phase 2
~Nov 2020
~Feb 2022
Phase 3
~May 2022
~Aug 2023
NDA/BLA
Nov 2023
Jan 2026
NDA/BLACurrent
NCT06447990
1,178 pts·NMOSD
2023-112026-01·Completed
1,178 total pts1 indication
Approved
CompletedCurrentUpcoming
Catalysts (1)
2026-01-152mo agoPh3 Readout· NMOSD
Trial Timeline
2024Q2Q3Q42025Q2Q3Q42026
NDA/BLA
Complet…
Catalysts
Ph3 Readout
2026-01-15 · 2mo ago
NMOSD
Completed|StartCompletionToday
Trials (1)
NCTPhaseIndicationStatusNEP
NCT06447990NDA/BLANMOSDCompleted1178LiverFat
Competitors (10)
DrugCompanyPhaseTargetMOA
VoxaderotideJohnson & JohnsonNDA/BLAPI3KαIL-13i
JNJ-8637Johnson & JohnsonNDA/BLACD20WEE1i
MRK-853Merck & CoPhase 1PRMT5WEE1i
RimamavacamtenMerck & CoPhase 1PI3KαDLL3 ADC
DoxafotisoranDaiichi SankyoPhase 1Cl18.2WEE1i
FixazanubrutinibAmgenPhase 2PI3KαCAR-T BCMA
369-789Hansoh PharmaPhase 3PI3KαTNFi
MavutuximabHansoh PharmaPhase 2/3PI3KαPCSK9i
TalatuximabSamsung BiologicsPreclinicalCD3WEE1i
SematenlimabSamsung BiologicsPhase 3PI3KαBCMA ADC