← Pipeline|Tixacagene

Tixacagene

Preclinical
RNA-5678
Source: Trial-derived·Trials: 1
Modality
mAb
MOA
DLL3 ADC
Target
SMN2
Pathway
DDR
MDSMSET
Development Pipeline
Preclinical
Oct 2020
Dec 2031
PreclinicalCurrent
NCT06202992
109 pts·MDS
2020-102031-12·Recruiting
109 total pts1 indication
Phase 1
Phase 2
Phase 3
NDA/BLA
Approved
CompletedCurrentUpcoming
Catalysts (1)
2031-12-145.7y awayInterim· MDS
Trial Timeline
Q42021Q2Q3Q42022Q2Q3Q42023Q2Q3Q42024Q2Q3Q42025Q2Q3Q42026Q2Q3Q42027Q2Q3Q42028Q2Q3Q42029Q2Q3Q42030Q2Q3Q42031Q2Q3Q4
Preclinical
Recruit…
Catalysts
Interim
2031-12-14 · 5.7y away
MDS
Recruiting|StartCompletionToday
Trials (1)
NCTPhaseIndicationStatusNEP
NCT06202992PreclinicalMDSRecruiting109EASI-75
Competitors (10)
DrugCompanyPhaseTargetMOA
NVS-4076NovartisPreclinicalTROP-2DLL3 ADC
RimamavacamtenMerck & CoPhase 1PI3KαDLL3 ADC
NVO-6275Novo NordiskPhase 1SMN2BTKi
TAK-5300TakedaPhase 1SMN2AuroraAi
AMG-9654AmgenPhase 2GPRC5DDLL3 ADC
GIL-2259Gilead SciencesApprovedSMN2CAR-T CD19
REG-647RegeneronPreclinicalSMN2SOS1i
OlpafutibatinibImmunocoreApprovedSMN2Menini
TixatapinarofArvinasPhase 1/2CDK2DLL3 ADC
GLP-3342GalapagosPhase 1/2PLK4DLL3 ADC