Thalassemia
1 programs · 1 companies
Programs
1
Companies
1
Trials
3
MOAs
1
CFTR Modulator
Drugs
| Drug | Company | Phase | Target | MOA |
|---|---|---|---|---|
| Exagamglogene autotemcel | Approved | BCL11A |
Trials (3)
| NCT | Drug | Phase | Status |
|---|---|---|---|
| NCT03876010 | Exagamglogene autotemcel | Approved | Terminated |
| NCT06650518 | Exagamglogene autotemcel | Approved | Terminated |
| NCT03037434 | Exagamglogene autotemcel | Approved | Terminated |