RA
Ultragenyx
RARE·NASDAQNovato CAFounded 20101,600 employees
Mid CapbiotechPublicRare DiseaseGenetic Medicine
Platform: ERT & Gene
Market Cap
$6B
All Drugs
4
Clinical Trials
7
Failed / Terminated
1
FDA Approved
1
Stock Price & Catalysts (RARE)
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Drug Pipeline (4 programs)
| Drug Name | Code | Phase | Trials | Modality | Target | MOA | Indications |
|---|---|---|---|---|---|---|---|
| RAR-1117 | RAR-1117 | Phase 1/2 | 2 | TYK2 | WMEndometrial Ca | ||
| Lisorapivir | RAR-6952 | Approved | 3 | AuroraA | Heart FailureUC | ||
| RAR-5994 | RAR-5994 | Phase 2/3 | 1 | IL-13 | GA | ||
| RAR-440 | RAR-440 | Phase 2 | 1 | FLT3 | MG |
SEC Filings & Financial Documents
Insider Trading Activity
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Catalyst Events (7)