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Harmony Bio

San Francisco CAFounded 202030 employees
Private CapbiotechPrivateRare Disease
Platform: Hemophilia Gene
Market Cap
N/A
All Drugs
4
Clinical Trials
5
Failed / Terminated
1
FDA Approved
1
Drug Pipeline (4 programs)
Drug NameCodePhaseTrialsModalityTargetMOAIndications
NidazumabHAR-6921Phase 21Gene EditingCFTRDLL3 ADCFabryIgAN
HAR-6503HAR-6503Approved2RadioligandCDK2RAS(ON)iMigraineCKD
TiratinibHAR-6515Preclinical1Gene EditingFLT3Anti-TauEndometrial CaBCC
HAR-9296HAR-9296Phase 11mAbCD19CD47iHNSCCCeliac
Financial Documents
This is a private company — SEC filings are not available.
Catalyst Events (3)
2025-08-08
Nidazumab Ph2 Data
Fabry
Past
2025-12-12
Tiratinib Interim
BCC
Past
2027-02-08
HAR-6503 Ph3 Readout
Migraine
Ph3 Readout